• Rare Case of Spinal Canal Narrowing Due to Amyloid Buildup Reported in FAP Patient
  • How New Caregivers Must Address Feelings of Denial
  • Age-related Changes in TTR Gene Expression May Explain Disease Differences Within Families, Study Suggests
  • Vyndaqel Safe But Generally Ineffective at Delaying FAP Neuropathy in Long Term, Study Suggests
  • Navigating the Turbulent Feelings of Caregiving
  • Longer Wait for Liver Transplant Can Worsen FAP Afterward, Study Finds
  • FAP Patient with Rare Mutation and Advancing Nerve, Heart Damage Treated Ably with Vyndaqel, Case Study Reports
  • Implanting Pacemaker Before Liver Transplant Does Not Lead to Better Outcomes, Study Reveals
  • Brexit Could Have Real Effects for UK Rare Disease Patients, Experts Warn
  • Moral Dilemmas Complicate Treatment of Rare Diseases, Says Israeli Bioethicist
  • NIH Rare Disease Day Highlights Joint Networks Advancing Array of Research
  • WODC 2019 Organizers Expect 1,200 to Attend Rare Disease Conference in April