• FAP Diagnosis Worth Considering in Patients with Neuropathy and Cardiac and Eye Issues, Case Report Shows
  • Researchers Report First Case of FAP with Chronic Dry Cough in Large Chinese Family
  • Liver Transplant, Vyndaqel Prolong Life of Early-stage FAP Patients, Study Reports
  • Val30Met FAP Patients’ Loss of Sensation Occurs in Both Upper and Lower Limbs, Study Reports
  • Lengthening of Amyloid Fibrils May Lead to Nerve Cell Loss in FAP Patients, Study Suggests
  • #NORDSummit – Major Issues on Table for Rare Disease Patients in US as Midterm Elections Approach
  • FAP Not Common in Patients with Charcot-Marie-Tooth Disease Type 2, Study Reports
  • Tegsedi and Onpattro May Ably Treat FAP, But Are Overpriced, ICER Reports
  • Tegsedi Approved in US for Treatment of FAP in Adults
  • Tegsedi Now Approved in Canada for FAP Treatment in Adults
  • Advocacy Groups, Doctors Question Rising Prices of Rare Disease Treatments
  • Alnylam Submits New Drug Application in Japan for Patisiran in Treatment of Hereditary ATTR Amyloidosis