• Patients, Family and Friends to Take Part in Variety of Rare Disease Day Events Worldwide
  • Eye Issues Still Prevalent in Val30Met FAP Patients After Liver Transplant, Study Shows
  • FDA Revising ‘Draft Guidance’ on Developing Treatments for Rare Diseases
  • Vyndaqel Is Safe, Effective for People with TTR-FAP, Review Study Suggests
  • Heart Problems Are Top Cause of Death for FAP Patients Who Had Liver Transplant, Study Says
  • Longer ATXN2 Coding Sequence Linked to Earlier TTR-FAP Onset in Val30Met Families, Study Shows
  • Vyndaqel May Help Halt Neurological Disease Progression in Patients With Val30Met Mutation, Study Reveals
  • Rising Healthcare Costs Strain EU Budgets Even as New Therapies Flourish
  • FAP Patients with Val30Met Mutation Exhibit Differences in Japan, Study Finds
  • Patients in France with FAP, Upper Limb Nerve Damage Often Misdiagnosed, Study Suggests
  • FAP Diagnosis Worth Considering in Patients with Neuropathy and Cardiac and Eye Issues, Case Report Shows
  • Researchers Report First Case of FAP with Chronic Dry Cough in Large Chinese Family