How Age of Onset Affects Disease Progression in FAP
Patients with familial amyloid polyneuropathy (FAP) may wonder how the age of onset of the symptoms relates to the progression of their disease. Here ... Read more
Updates
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New Streaming Channel Showcases Rare Disease Films
When the COVID-19 pandemic forced the postponement of a rare disease film festival originally slated for May, its organizers set out to find a ... Read more -
FAP and Your Heart
If you have familial amyloid polyneuropathy (FAP), a progressive neurodegenerative disease, your doctor has probably talked to you about screening for problems with your heart. ... Read more -
Tegsedi Eases Disease Progression in FAP Patients, Trial Data Show
Treatment with Tegsedi (inotersen) slows neurological disease progression in people with familial amyloid polyneuropathy (FAP), results from a Phase 2/3 clinical trial show. The ... Read more -
FAP and Your Eyes
Familial amyloid polyneuropathy (FAP) is a disorder in which abnormal clumps of proteins called TTR amyloids accumulate in tissues and organs, interfering with their ... Read more
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Tafamidis Delays Disease Progression in Patients with Transthyretin Amyloid Polyneuropathy, Pfizer Study Suggests
News
An interim analysis of the Phase 3 trial for tafamidis (Fx-1006A) as a therapy for patients with hereditary transthyretin amyloid polyneuropathy (TTR-FAP) shows the investigational treatment delays disease progression, Pfizer announced. The study, “Long-term safety and efficacy of tafamidis for ... Read more