• Patient Advocacy Groups Worldwide Plan Events to Mark Rare Disease Day, Feb. 28
  • Taiwanese Team Develops Mouse Model That Displays the Early Stages of Human FAP
  • Rare Disease Groups, Patients Differ on ‘Right to Try’ Bill Before US Congress
  • Changes in Walking Patterns Could Help Predict FAP, Portuguese Study Reports
  • NORD Fundraiser Sets 7,000-Mile ‘Bike, Run or Walk’ Goal for 7,000 Rare Diseases
  • Japanese Experts Develop Guidelines for the Country’s Unique TTR-FAP Variations
  • Vyndaqel May Not Protect FAP Patients Against Anemia, Study Finds
  • Alnylam Continuing FAP Treatment Development Without Former Partner Sanofi
  • Inotersen a Step Closer to Approval as FDA Grants Priority Review to Ionis’ NDA
  • Surgical Joint Fusion Is Effective Treatment for Rare Knee Deformity in FAP, Case Report Shows
  • Researchers Come Up with Tool Kit of Tests for Early Diagnosis of TTR-FAP
  • Prevalence Study Finds FAP May Be More Common Worldwide Than Previously Thought